Stanford University 3rd Annual Spinal Muscular Atrophy Continuing Medical Education Conference on Clinical Decision-Making in the Midst of an Unfolding Phenotype

Continuing medical education and training is building momentum among the healthcare community treating and managing individuals with SMA.  In this era of disease-modifying treatments, evolving SMA phenotypes are unfolding and clinical decision-making is requiring greater attention for the most optimal outcomes.  Multidisciplinary medical and rehabilitative management recommendations are sought after while weighing the treatment options, long term outcomes, and ethical considerations to effectively treat and manage patients with SMA.  We intend to continue to enhance the knowledge and understanding of healthcare providers including physicians, specialists, physical, occupational, and speech language pathologist and nurses, outside specialized centers, in the clinical decision-making and medical and rehabilitative management of individuals with SMA. 

This virtual 3-day brunch seminar series is provided to (1) integrate new 2021 treatment advances into clinical decision-making; and (2) use new SMA standards as a model for public health, primary and multi-disciplinary care of all children and adults with neuromuscular disease. 

For each day, the 3-hour seminar will involve an educational lecture series providing an overview of SMA therapeutic treatment updates and clinical decision-making for optimal outcomes, the impact of newborn screening, as well as primary and multi-disciplinary care for children and adults living with SMA.  Didactics will be followed by an in depth review of rehabilitation evidence, with a specific focus on multidisciplinary clinical case discussions.  The sessions will include opportunities for clinical decision-making for the evolving phenotypes as well as a shared session to support multi-disciplinary providers to medically manage and develop rehabilitation programs and episodes of care including evaluations, goals, interventions and strategies to exercise.

At the end of this conference, participants will have an understanding of the current advances in therapeutic treatments, clinical, and rehabilitative management in SMA. Attendees will understand opportunities available to enhance clinical care, determine the most appropriate treatment, medical and rehabilitative interventions, and contemplate the ethical debates to treatment and management.

A Call for Clinical Cases!
Click here to submit your case to be reviewed during the live webinar

Registration is closing at 2pm on Wednesday, December 1st.  After 2pm, if you would like to register, please email [email protected] and [email protected].  We will need to manually register you and send you the appropriate log in details. 

We will be utilizing Pheedloop, a virtual platform, for the conference.  An invitation to the the platform will be sent out one week prior to the conference.  Registration fee includes course materials and certificate of participation.

*Please note: The conference will take place in Pacific Standard Time (PST)*

Early Bird Rate: 

Physicians - $175
International Physicians - $140
Nurses/AHPs - $125
International Nurses/AHPs - $100
California Children's Services/Public Health Providers/Administrators/Staff - $125
Industry- $275
Trainees/Residents - $75 

Rate After 11/04/21: 

Physicians - $225
International Physicians - $180
Nurses/AHPs - $175
International Nurses/AHPs - $140
California Children's Services/Public Health Providers/Administrators/Staff - $175
Industry- $350
Trainees/Residents - $75 

Your email address is used for critical information, including registration confirmation, evaluation, and certificate. Be sure to include an email address that you check frequently.

STAP-eligible employees can use STAP funds towards the registration fees for this activity.  Complete the STAP Reimbursement Request Form and submit to your department administrator. 

1. Summarize the advancements and barriers of providing therapeutic treatments for individuals with SMA.
2. Recognize and discuss the impact of newborn screening, primary, and multi-disciplinary clinical care for children and adults with SMA in this era of evolving phenotypes and therapeutics.
3. Determine and select suitable rehabilitation programs based on evidence and clinical decision-making for optimal outcomes including standards of care recommendations.

In support of improving patient care, Stanford Medicine is jointly accredited by the Accreditation Council for Continuing Medical Education (ACCME), the Accreditation Council for Pharmacy Education (ACPE), and the American Nurses Credentialing Center (ANCC), to provide continuing education for the healthcare team.  

Credit Designation 

American Medical Association (AMA) 

Stanford Medicine designates this Live Activity for a maximum of 8.00 AMA PRA Category 1 Credits^TM.  Physicians should claim only the credit commensurate with the extent of their participation in the activity. 

Stanford Health Care Department of Rehabilitation is an approved provider for physical therapy, occupational therapy, and speech language pathology for courses that meet the requirements set forth by the respective Boards. This course is approved for 8.00 hour(s) CEU for PT, OT and SLP.

Cancellation Policy
Cancellations received in writing no less than 20 days before the course will be refunded, less a 20% administrative fee. No refunds will be made on cancellations received after that date. Please send cancellation requests to [email protected].

Stanford University School of Medicine reserves the right to cancel or postpone this program if necessary; in the event of cancellation, course fees will be fully refunded. We are not responsible for other costs incurred such as non-refundable airline tickets or hotel penalties.

Accessibility Statement
 Stanford University School of Medicine is committed to ensuring that its programs, services, goods and facilities are accessible to individuals with disabilities as specified under Section 504 of the Rehabilitation Act of 1973 and the Americans with Disabilities Amendments Act of 2008.  If you have needs that require special accommodations, please contact the CME Conference Coordinator.

Cultural and Linguistic Competency
The planners and speakers of this CME activity have been encouraged to address cultural issues relevant to their topic area for the purpose of complying with California Assembly Bill 1195. Moreover, the Stanford University School of Medicine Multicultural Health Portal contains many useful cultural and linguistic competency tools including culture guides, language access information and pertinent state and federal laws.  You are encouraged to visit the Multicultural Health Portal: https://laneguides.stanford.edu/multicultural-health

For activity related questions, please contact
     Name: Melissa Schwartz
     Title: Events Project Manager
     Email: [email protected]

For CME general questions, please contact 
     Email: [email protected]

Mitigation of Relevant Financial Relationships

Stanford Medicine adheres to the Standards for Integrity and Independence in Accredited Continuing Education.

There are no relevant financial relationships with ACCME-defined ineligible companies for anyone who was in control of the content of this activity, except those listed in the below table. All of the relevant financial relationships listed for these individuals have been mitigated. 

Member Information

Role in activity

Nature of Relationship(s) / Name of Ineligible Company(s)

Ana Tesi Tesi Rocha, MD
Clinical Associate Professor, Pediatric Neurology & Neurological Science
Stanford University Medical Center

Co-Course Director, Faculty

Advisor-Biogen Idec (Relationship has ended)|Advisor-Novartis AG (Relationship has ended)|Honoraria-Roche (Relationship has ended)|Honoraria-Genentech, Inc. (Relationship has ended)|Honoraria-Sarepta (Relationship has ended)

John W Day, MD, PhD
Professor of Neurology and Pediatrics (Genetics) and by courtesy, Pathology
Stanford University Medical Center

Course Director, Faculty

Grant or research support-Audentes|Grant or research support-Biogen|Grant or research support-Cytokinetics|Grant or research support-Ionis Pharmaceuticals|Grant or research support-Novartis Gene Therapies|Grant or research support-Pfizer, Inc.|Grant or research support-Roche|Grant or research support-Sanofi-Genzyme|Grant or research support-Sarepta Therapeutics|Grant or research support-Scholar Rock|Membership on Advisory Committees or Review Panels, Board Membership, etc.-AMO Pharmaceuticals|Membership on Advisory Committees or Review Panels, Board Membership, etc.-Avidity Therapeutics|Membership on Advisory Committees or Review Panels, Board Membership, etc.-Biogen|Membership on Advisory Committees or Review Panels, Board Membership, etc.-Cytokinetics|Membership on Advisory Committees or Review Panels, Board Membership, etc.-Novartis|Membership on Advisory Committees or Review Panels, Board Membership, etc.-Novartis Gene Therapies|Membership on Advisory Committees or Review Panels, Board Membership, etc.-Roche/Genentech Pharmaceuticals|Membership on Advisory Committees or Review Panels, Board Membership, etc.-Sarepta Therapeutics|Membership on Advisory Committees or Review Panels, Board Membership, etc.-Scholar Rock|Consulting Fee-Affinia Therapeutics|Consulting Fee-Audentes Therapeutics|Consulting Fee-Ionis Pharmaceuticals|Consulting Fee-Pfizer, Inc.|Royalties or Patent Beneficiary-Athena Diagnostics

Susan Apkon, MD
Professor, Department of Physical Medicine and Rehabilitation
University of Colorado School of Medicine

Faculty

Membership on Advisory Committees or Review Panels, Board Membership, etc.-Sarepta Therapeutics (Relationship has ended)|Grant or research support-Sarepta|Membership on Advisory Committees or Review Panels, Board Membership, etc.-Dyne (Relationship has ended)|Grant or research support-Biogen|Grant or research support-Novartis/AVXS|Grant or research support-Scholar Rock

Cathy Barsotti-Dooling

Faculty

Advisor-Genentech SMA Link advisory committee

Max Brown, other
n/a

Faculty

Nothing to disclose

Diana Castro, MD
Associate Professor, Departments of Pediatrics and Neurology
UT Southwestern Medical Center

Faculty

Advisor-Biogen Idec (Relationship has ended)|Grant or research support-Biogen Idec|Advisor-Novartis AG (Relationship has ended)|Advisor-Roche (Relationship has ended)

Wendy K Chung, MD, PhD
Chief, Division of Clinical Genetics, Department of Pediatrics
Columbia University Irving Medical Center

Faculty

Nothing to disclose

Emma Ciafaloni, MD
Professor of Neurology and Pediatrics
University of Rochester Medical Center

Faculty

Consulting Fee-Biogen Idec (Relationship has ended)|Advisor-Alexion|Honoraria-Ology (Relationship has ended)|Consulting Fee-Sarepta (Relationship has ended)|Honoraria-Amicus (Relationship has ended)|Advisor-Viela

Miranda Clements, MS, CCC-SLP
Speech-Language Pathologist
Lucile Packard Children’s Hospital at Stanford

Faculty

Nothing to disclose

Basil Darras, MD
Associate Neurologist-in-Chief; Chief, Division of Clinical Neurology; Director, Neuromuscular Center and Spinal Muscular Atrophy Program, Professor of Neurology
Harvard Medical School

Faculty

Grant or research support-NIH |Grant or research support-National Inst. of Neuro Disorders and Stroke |Grant or research support-Slaney Fund for SMA |Grant or research support-Spinal Muscular Atrophy Foundation|Grant or research support-CureSMA|Grant or research support-Working on Walking Fund |Grant or research support-Ionis Pharmaceuticals Inc. (studies ENDEAR, CHERISH, CS2/CS12 studies|Grant or research support-Biogen for CS11 Study|Grant or research support-AveXis|Grant or research support-Sarepta Pharmaceuticals|Grant or research support-PTC Therapeutics|Grant or research support-Roche|Grant or research support-Scholar Rock |Grant or research support-Fibrogen

Matt Dooling, BS

Faculty

Nothing to disclose

Morgan J Duffy, MSc
Head of Strategy and Operations
OneFifteen

Faculty

Employment-Verily Life Sciences

Timothy Estilow, OTR/L
Occupational Therapist, Occupational Therapy Department
The Children's Hospital of Philadelphia

Faculty

Speakers Bureau-Sarepta Therapeutics

Richard Finkel, MD
Director of Translational Neuroscience Research
St. Jude Children's Research Hospital

Faculty

Membership on Advisory Committees or Review Panels, Board Membership, etc.-AveXis (Relationship has ended)|Membership on Advisory Committees or Review Panels, Board Membership, etc.-Biogen Idec|Membership on Advisory Committees or Review Panels, Board Membership, etc.-Capricor (Relationship has ended)|Membership on Advisory Committees or Review Panels, Board Membership, etc.-Catabasis (Relationship has ended)|Royalties or Patent Beneficiary-Children's Hospital of Philadelphia|Royalties or Patent Beneficiary-Elsevier|Advisor-n-Lorem Foundation|Membership on Advisory Committees or Review Panels, Board Membership, etc.-Novartis AG|Membership on Advisory Committees or Review Panels, Board Membership, etc.-ReveraGen|Membership on Advisory Committees or Review Panels, Board Membership, etc.-Roche|Membership on Advisory Committees or Review Panels, Board Membership, etc.-Scholar Rock

Jenny Gheith

Faculty

Nothing to disclose

Jessica Guzman, RN, PHN
Pediatric Neuromuscular Nurse Coordinator
Lucile Packard Children’s Hospital at Stanford

Faculty

Advisor-SAREPTA (Relationship has ended)|Advisor-Novartis AG (Relationship has ended)

Tim Hagenacker, MD
Department of Neurology
University Hospital Essen, University of Duisburg-Essen
Germany

Faculty

Advisor-Biogen Idec|Honoraria-Biogen Idec|Grant or research support-Biogen Idec|Advisor-Roche|Honoraria-Roche|Grant or research support-Roche|Grant or research support-Novartis AG|Honoraria-Novartis AG (Relationship has ended)

Kristin Krosschell, DPT
Professor of Physical Therapy and Human Movement Sciences and Pediatrics
Northwestern University Feinberg School of Medicine

Faculty

Advisor-Biogen Idec|Advisor-Genentech, Inc.|Grant or research support-Biogen Idec|Grant or research support-Scholar Rock subcontract via Lurie Children's|Grant or research support-Avexis/Novartis subcontract via Lurie Children's (Relationship has ended)|Consulting Fee-Aspa Therapeutics|Consulting Fee-Cure SMA

Natalie Lamb, RN

Faculty

Nothing to disclose

Yoni Levy

Faculty

Nothing to disclose

Katlyn Elizabeth McGrattan, PhD
Assistant Professor, Department of Speech-Language-Hearing Sciences
University of Minnesota

Faculty

Employment-University of Minnesota|Employment-Masonic Children's Hospital|Consulting Fee-Biogen Idec|Consulting Fee-Novartis AG|Consulting Fee-Roche

Nancy Mendelsohn, MD
Senior Vice President Medical Affairs Genetics & Rare Diseases
United Health Group

Faculty

Nothing to disclose

Jacqueline Montes, PT, EdD, NCS
Assistant Professor of Rehabilitation and Regenerative Medicine in the Program for Physical Therapy
Columbia University Irving Medical Center

Faculty

Advisor-Biogen Idec|Consulting Fee-Roche|Advisor-Genentech, Inc.|Advisor-Scholar Rock|Advisor-Sarepta

Meghan Moore Burk, PT, DPT, NCS
Physical Therapist
Department of Physical Therapy, Children’s Hospital Colorado

Faculty

Membership on Advisory Committees or Review Panels, Board Membership, etc.-Genentech, Inc. (Relationship has ended)|Consulting Fee-Biogen Idec

Julie Muccini, Other
Occupational Therapist, Clinical Research Manager, Human Performance Lab
Stanford University

Faculty

Nothing to disclose

Julie Parsons, MD
Professor of Clinical Pediatrics and Neurology
University of Colorado School of Medicine

Faculty

Grant or research support-Biogen Idec|Grant or research support-Novartis AG|Grant or research support-PTC Therapeutics|Grant or research support-Scholar Rock|Advisor-Biogen Idec|Advisor-Scholar Rock|Advisor-Novartis AG

Amy Pasternak, PT, DPT, PCS
Department of Physical Therapy
Boston Children's Hospital

Faculty

Advisor-Roche (Relationship has ended)

Catherine Pedersen, BA

Faculty

Nothing to disclose

Crystal M Proud, MD
Director, Neurology and Director, Neuromuscular Clinic and Spinal Muscular Atrophy Center
Children's Hospital of The King's Daughters (CHKD)

Faculty

Speakers Bureau-Biogen Idec|Membership on Advisory Committees or Review Panels, Board Membership, etc.-Biogen Idec|Membership on Advisory Committees or Review Panels, Board Membership, etc.-Sarepta|Membership on Advisory Committees or Review Panels, Board Membership, etc.-Novartis AG|Membership on Advisory Committees or Review Panels, Board Membership, etc.-F. Hoffmann La Roche Ltd.|Membership on Advisory Committees or Review Panels, Board Membership, etc.-Scholar Rock|Grant or research support-Biogen Idec|Grant or research support-Novartis AG|Grant or research support-AMO|Grant or research support-Astellas|Grant or research support-CSL Behring|Grant or research support-Fibrogen|Grant or research support-PTC|Grant or research support-Pfizer, Inc.|Grant or research support-Sarepta|Grant or research support-Scholar Rock

Lee Sanders, MD
Associate Professor of Pediatrics (General Pediatrics) and, by courtesy, or Epidemiology and Population Health
Stanford University

Faculty

Paid consultant-Anthem AI

Christa Saul, AA
Na

Faculty

Nothing to disclose

Perry B Shieh, MD, PhD
Associate Professor of Neurology
UCLA

Faculty

Consulting Fee-Sarepta Therapeutics (Relationship has ended)|Speakers Bureau-Grifols|Speakers Bureau-CSL Behring|Speakers Bureau-Alexion|Speakers Bureau-Catalyst|Speakers Bureau-Genentech, Inc.|Speakers Bureau-Biogen Idec|Consulting Fee-Pfizer, Inc. (Relationship has ended)|Consulting Fee-Novartis AG (Relationship has ended)|Consulting Fee-Biogen Idec (Relationship has ended)|Consulting Fee-Genentech, Inc. (Relationship has ended)|Consulting Fee-Alexion (Relationship has ended)|Grant or research support-Biogen Idec|Grant or research support-Novartis AG|Grant or research support-Sarepta|Grant or research support-Pfizer, Inc.|Grant or research support-Audentes|Grant or research support-Genzyme Corporation|Grant or research support-PTC|Grant or research support-Catalyst|Grant or research support-SOLID Biosciences|Grant or research support-Fulcrum|Grant or research support-AMO Pharm

Charlotte J Sumner, MD
Professor of Neurology, Departments of Neurology and Neuroscience
The Johns Hopkins University School of Medicine

Faculty

Honoraria-Biogen Idec|Consulting Fee-Novartis AG|Consulting Fee-Scholar Rock|Consulting Fee-Epirium|Consulting Fee-GenEdit|Consulting Fee-Atalanta|Consulting Fee-Nura Bio|Grant or research support-Roche|Grant or research support-Biogen Idec|Grant or research support-Argenx|Consulting Fee-Alnylam Pharmaceuticals (Relationship has ended)

Eduardo F Tizzano , MD, PhD
Director
Hospital Universitari Vall d’Hebron, Area Genetica Clinica i Molecular (HUVH), Medicine Genetics Research Group (VHIR)
Spain

Faculty

Advisor-Biogen Idec|Advisor-Novartis AG|Advisor-Roche|Grant or research support-Biogen Idec|Grant or research support-Roche|Consulting Fee-Biogen Idec|Consulting Fee-Novartis AG|Consulting Fee-Roche

Karolina Watson, MS
Nurse Practitioner
Stanford University Medical Center

Faculty

Nothing to disclose

Sally Dunaway Young, PT, DPT
Physical Therapist, Clinical Research Manager, Division of Neuromuscular Medicine
Stanford University Medical Center

Faculty, Planner

Advisor-Biogen Idec|Advisor-Roche|Advisor-Scholar Rock|Consulting Fee-Cure SMA|Grant or research support-Cure SMA

Tina Duong, PT, PhD
Physical Therapist, Sr. Research Scientist, Division of Neuromuscular Medicine
Stanford University Medical Center

Faculty, Planner

Consulting fees-Roche|Advisory Board-Biogen Idec|Advisory Board-Novartis AG

Richard S Gee, PT
Physical Therapist
Lucile Packard Children’s Hospital at Stanford

Faculty, Planner

Consulting Fee-Biogen Idec|Consulting Fee-Roche

Connie Wolford, MSN, FNP-BC
Nurse Practitioner
Stanford University School of Medicine

Faculty, Planner

Speakers Bureau-Biogen Idec|Advisor-Biogen Idec

Dana McDonnell, MS
Clinical Research Coordinator
Stanford University

Planner

Nothing to disclose

Dong Nguyen, MA
Administrative Associate
Stanford University

Planner

Nothing to disclose

Whitney Tang
Clinical Research Coordinator
Stanford University

Planner

Nothing to disclose

Kathie S Lin, MD
Clinical Assistant Professor, Neurology & Neurological Sciences
Stanford University

Reviewer

Nothing to disclose

COMMERCIAL SUPPORT ACKNOWLEDGEMENT
This CME Activity is supported in part by educational grants from Cytokinetics, Inc., Genentech, a member of the Roche Group, Ionis Pharmaceuticals, Inc., Muscular Dystrophy Association, Novartis Gene Therapies, Inc., and Scholar Rock Inc.